See what the lab has been up to in the media Penn Med, Children’s Hospital of Philadelphia receive $14 million grant for gene-editing research Read More Here New FDA Designations May Jumpstart Gene Therapy Development Read More Here Children's Hospital of Philadelphia Researchers Report Encouraging First Evidence of Effective New Gene Therapy to Treat Multiple Sulfatase Deficiency Read More Here Elucidating Shared Mechanisms of Pediatric and Adult Neurodegeneration Read More Here